Search Results - Simone Morando
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Determining minimal clinically important differences in the Hammersmith Functional Motor Scale Expanded for untreated spinal muscular atrophy patients: An international study by Giorgia Coratti, Francesca Bovis, Maria Carmela Pera, Mariacristina Scoto, Jacqueline Montes, Amy Pasternak, Anna Mayhew, Robert Muni‐Lofra, Tina Duong, Annemarie Rohwer, Sally Dunaway Young, Matthew Civitello, Francesca Salmin, Irene Mizzoni, Simone Morando, Marika Pane, Emilio Albamonte, Adele D'Amico, Noemi Brolatti, Maria Sframeli, Chiara Marini‐Bettolo, Valeria Ada Sansone, Claudio Bruno, Sonia Messina, Enrico Bertini, Giovanni Baranello, John Day, Basil T. Darras, Darryl C. De Vivo, Michio Hirano, Francesco Muntoni, Richard Finkel, Eugenio Mercuri
Published 2024Get full text
Artículo Open Access -
2
Longitudinal Assessment of 4‐Year HFMSE Changes in SMA II and III Patients Treated With Nusinersen by Giorgia Coratti, Francesca Bovis, Marika Pane, Amy Pasternak, Emilio Albamonte, Irene Mizzoni, Allan M. Glanzman, Simone Morando, Jacqueline Montes, Ilaria Cavallina, Sally Dunaway Young, Tina Duong, Enrica Rolle, Matthew Civitello, Roberto De Sanctis, Chiara Bravetti, Federica Ricci, Giulio Gadaleta, Tiziana Mongini, Maria Sframeli, Maria Carmela Pera, Sonia Messina, Adele D'Amico, Michela Catteruccia, Noemi Brolatti, Michio Hirano, Zarazuela Zolkipli‐Cunningham, Basil T. Darras, Enrico Bertini, Claudio Bruno, John Day, Valeria A. Sansone, Richard S. Finkel, Eugenio Mercuri
Published 2025Get full text
Artículo Open Access -
3
Long‐term natural history in type II and III spinal muscular atrophy: a 4‐year international study on the Hammersmith Functional Motor Scale Expanded by Giorgia Coratti, Francesca Bovis, Maria Carmela Pera, Matthew Civitello, Annemarie Rohwer, Francesca Salmin, Allan M. Glanzman, Jacqueline Montes, Amy Pasternak, Roberto De Sanctis, Sally Dunaway Young, Tina Duong, Irene Mizzoni, Evelin Milev, Maria Sframeli, Simone Morando, Emilio Albamonte, Adele D'Amico, Michela Catteruccia, Noemi Brolatti, Marika Pane, Mariacristina Scoto, Sonia Messina, Jesica Exposito Escudero, Liesbeth De Waele, Michio Hirano, Zarazuela Zolkipli‐Cunningham, Basil T. Darras, Enrico Bertini, Andres Nascimiento Osorio, Claudio Bruno, Natalie Goemans, Valeria A. Sansone, John Day, Giovanni Baranello, Francesco Muntoni, Richard Finkel, Eugenio Mercuri
Published 2024Get full text
Artículo Open Access