Designing an exploratory phase 2b platform trial in NASH with correlated, co-primary binary endpoints
Fuente:
arXiv
Enregistré dans:
| Auteurs principaux: | Meyer, Elias Laurin, Mesenbrink, Peter, Di Prospero, Nicholas A., Pericàs, Juan M., Glimm, Ekkehard, Ratziu, Vlad, Sena, Elena, König, Franz |
|---|---|
| Format: | Preprint |
| Publié: |
2022
|
| Sujets: | |
| Accès en ligne: | |
| Tags: |
Ajouter un tag
Pas de tags, Soyez le premier à ajouter un tag!
|
Documents similaires
Exact matching as an alternative to propensity score matching
par: Glimm, Ekkehard, et autres
Publié: (2025)
par: Glimm, Ekkehard, et autres
Publié: (2025)
A novel longitudinal rank-sum test for multiple primary endpoints in clinical trials: Applications to neurodegenerative disorders
par: Xu, Xiaoming, et autres
Publié: (2024)
par: Xu, Xiaoming, et autres
Publié: (2024)
Futility Analysis under Scrutiny
par: Jin, Rui, et autres
Publié: (2025)
par: Jin, Rui, et autres
Publié: (2025)
Optimal allocation strategies in platform trials
par: Roig, Marta Bofill, et autres
Publié: (2023)
par: Roig, Marta Bofill, et autres
Publié: (2023)
Rank-based estimators of global treatment effects for cluster randomized trials with multiple endpoints
par: Smith, E. Davies, et autres
Publié: (2024)
par: Smith, E. Davies, et autres
Publié: (2024)
Evaluating amyloid-beta as a surrogate endpoint in trials of anti-amyloid drugs in Alzheimer's disease: a Bayesian meta-analysis
par: Ren, Sa, et autres
Publié: (2025)
par: Ren, Sa, et autres
Publié: (2025)
A comparison of methods for designing hybrid type 2 cluster-randomized trials with continuous effectiveness and implementation endpoints
par: Owen, Melody, et autres
Publié: (2025)
par: Owen, Melody, et autres
Publié: (2025)
While-alive regression analysis of composite survival endpoints
par: Fang, Xi, et autres
Publié: (2025)
par: Fang, Xi, et autres
Publié: (2025)
NCC: An R-package for analysis and simulation of platform trials with non-concurrent controls
par: Krotka, Pavla, et autres
Publié: (2023)
par: Krotka, Pavla, et autres
Publié: (2023)
Using shrinkage methods to estimate treatment effects in overlapping subgroups in randomized clinical trials with a time-to-event endpoint
par: Wolbers, Marcel, et autres
Publié: (2024)
par: Wolbers, Marcel, et autres
Publié: (2024)
Prediction intervals for overdispersed binomial endpoints and their application to toxicological historical control data
par: Menssen, Max, et autres
Publié: (2024)
par: Menssen, Max, et autres
Publié: (2024)
Visualizing the treatment effect on kidney hierarchical composite endpoints: From mosaic to maraca plots
par: Karpefors, Martin, et autres
Publié: (2025)
par: Karpefors, Martin, et autres
Publié: (2025)
Microbial correlation: a semi-parametric model for investigating microbial co-metabolism
par: Shi, Haoran, et autres
Publié: (2025)
par: Shi, Haoran, et autres
Publié: (2025)
Optimal allocation of trials to sub-regions in crop variety testing with multiple years and correlated genotype effects
par: Prus, Maryna, et autres
Publié: (2026)
par: Prus, Maryna, et autres
Publié: (2026)
Use of surrogate endpoints in health technology assessment: a review of selected NICE technology appraisals in oncology
par: Wheaton, Lorna, et autres
Publié: (2024)
par: Wheaton, Lorna, et autres
Publié: (2024)
Nonparametric estimation of an optimal treatment rule with fused randomized trials and missing effect modifiers
par: Williams, Nicholas, et autres
Publié: (2025)
par: Williams, Nicholas, et autres
Publié: (2025)
Assessing treatment efficacy for interval-censored endpoints using multistate semi-Markov models fit to multiple data streams
par: Morsomme, Raphael, et autres
Publié: (2025)
par: Morsomme, Raphael, et autres
Publié: (2025)
The role of randomization inference in unraveling individual treatment effects in early phase vaccine trials
par: Chen, Zhe, et autres
Publié: (2023)
par: Chen, Zhe, et autres
Publié: (2023)
Cristiano Ronaldo or Lionel Messi, who is more consistent in scoring goals? The evidence from CFM exploratory analysis
par: Anwar, Samsul, et autres
Publié: (2026)
par: Anwar, Samsul, et autres
Publié: (2026)
A response-adaptive multi-arm design for continuous endpoints based on a weighted information measure
par: Caruso, Gianmarco, et autres
Publié: (2024)
par: Caruso, Gianmarco, et autres
Publié: (2024)
Scaling behavioral incentives for low-carbon mobility through digital platforms
par: Liu, Bing, et autres
Publié: (2025)
par: Liu, Bing, et autres
Publié: (2025)
Shared Keyboard: An improved Bayesian design for phase I clinical trials via Beta kernel process
par: Zhao, Jiangyan, et autres
Publié: (2026)
par: Zhao, Jiangyan, et autres
Publié: (2026)
Mosqlimate: a platform to providing automatable access to data and forecasting models for arbovirus disease
par: Ganem, Fabiana, et autres
Publié: (2024)
par: Ganem, Fabiana, et autres
Publié: (2024)
Equipoise calibration of clinical trial design
par: Rigat, Fabio
Publié: (2025)
par: Rigat, Fabio
Publié: (2025)
Uncovering migration systems through spatio-temporal tensor co-clustering
par: Almquist, Zack W., et autres
Publié: (2021)
par: Almquist, Zack W., et autres
Publié: (2021)
Early developmental carry‐over effects on exploratory behaviour and DNA methylation in wild great tits (Parus major)
par: Bernice Sepers, et autres
Publié: (2024)
par: Bernice Sepers, et autres
Publié: (2024)
Model-based indicators for co-clustered environments and species communities
par: Scherting, Braden, et autres
Publié: (2025)
par: Scherting, Braden, et autres
Publié: (2025)
Shotgun DNA sequencing evidence: sample-specific and unknown genotyping error probabilities
par: Andersen, Mikkel Meyer
Publié: (2025)
par: Andersen, Mikkel Meyer
Publié: (2025)
On misconceptions about the Brier score in binary prediction models
par: Hoessly, Linard
Publié: (2025)
par: Hoessly, Linard
Publié: (2025)
Evaluation of clinical utility in emulated clinical trials
par: Hruza, Johannes, et autres
Publié: (2025)
par: Hruza, Johannes, et autres
Publié: (2025)
Incorporating estimands into meta-analyses of clinical trials
par: Remiro-Azócar, Antonio, et autres
Publié: (2025)
par: Remiro-Azócar, Antonio, et autres
Publié: (2025)
tsbootstrap: Enhancing Time Series Analysis with Advanced Bootstrapping Techniques
par: Gilda, Sankalp, et autres
Publié: (2024)
par: Gilda, Sankalp, et autres
Publié: (2024)
Yield forecasting based on short time series with high spatial resolution data
par: Pokal, Sayli, et autres
Publié: (2024)
par: Pokal, Sayli, et autres
Publié: (2024)
The Bayesian optimal two-stage design for clinical phase II trials based on Bayes factors
par: Kelter, Riko, et autres
Publié: (2025)
par: Kelter, Riko, et autres
Publié: (2025)
Monitoring overall survival in pivotal trials in indolent cancers
par: Fleming, Thomas R, et autres
Publié: (2023)
par: Fleming, Thomas R, et autres
Publié: (2023)
Benchmarking covariate-adjustment strategies for randomized clinical trials
par: Shao, Yulin, et autres
Publié: (2026)
par: Shao, Yulin, et autres
Publié: (2026)
Mixed additive modelling of global alien species co-invasions of plants and insects
par: Boschi, Martina, et autres
Publié: (2023)
par: Boschi, Martina, et autres
Publié: (2023)
Generalizing conditional average treatment effects from nested randomized trials to all trial-eligible individuals
par: Wen, Lan, et autres
Publié: (2026)
par: Wen, Lan, et autres
Publié: (2026)
Negative correlations in Ising models of credit risk
par: Emonti, Chiara, et autres
Publié: (2025)
par: Emonti, Chiara, et autres
Publié: (2025)
Clinical trials with interim analyses: Standardizing Terminology to increase clarity
par: Asikanius, Elina, et autres
Publié: (2024)
par: Asikanius, Elina, et autres
Publié: (2024)
Documents similaires
-
Exact matching as an alternative to propensity score matching
par: Glimm, Ekkehard, et autres
Publié: (2025) -
A novel longitudinal rank-sum test for multiple primary endpoints in clinical trials: Applications to neurodegenerative disorders
par: Xu, Xiaoming, et autres
Publié: (2024) -
Futility Analysis under Scrutiny
par: Jin, Rui, et autres
Publié: (2025) -
Optimal allocation strategies in platform trials
par: Roig, Marta Bofill, et autres
Publié: (2023) -
Rank-based estimators of global treatment effects for cluster randomized trials with multiple endpoints
par: Smith, E. Davies, et autres
Publié: (2024)