PepMLM: Target Sequence-Conditioned Generation of Therapeutic Peptide Binders via Span Masked Language Modeling

Fuente: arXiv
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Autori principali: Chen, Tianlai, Dumas, Madeleine, Watson, Rio, Vincoff, Sophia, Peng, Christina, Zhao, Lin, Hong, Lauren, Pertsemlidis, Sarah, Shaepers-Cheu, Mayumi, Wang, Tian Zi, Srijay, Divya, Monticello, Connor, Vure, Pranay, Pulugurta, Rishab, Kholina, Kseniia, Goel, Shrey, DeLisa, Matthew P., Truant, Ray, Aguilar, Hector C., Chatterjee, Pranam
Natura: Preprint
Pubblicazione: 2023
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author Chen, Tianlai
Dumas, Madeleine
Watson, Rio
Vincoff, Sophia
Peng, Christina
Zhao, Lin
Hong, Lauren
Pertsemlidis, Sarah
Shaepers-Cheu, Mayumi
Wang, Tian Zi
Srijay, Divya
Monticello, Connor
Vure, Pranay
Pulugurta, Rishab
Kholina, Kseniia
Goel, Shrey
DeLisa, Matthew P.
Truant, Ray
Aguilar, Hector C.
Chatterjee, Pranam
author_facet Chen, Tianlai
Dumas, Madeleine
Watson, Rio
Vincoff, Sophia
Peng, Christina
Zhao, Lin
Hong, Lauren
Pertsemlidis, Sarah
Shaepers-Cheu, Mayumi
Wang, Tian Zi
Srijay, Divya
Monticello, Connor
Vure, Pranay
Pulugurta, Rishab
Kholina, Kseniia
Goel, Shrey
DeLisa, Matthew P.
Truant, Ray
Aguilar, Hector C.
Chatterjee, Pranam
contents Target proteins that lack accessible binding pockets and conformational stability have posed increasing challenges for drug development. Induced proximity strategies, such as PROTACs and molecular glues, have thus gained attention as pharmacological alternatives, but still require small molecule docking at binding pockets for targeted protein degradation. The computational design of protein-based binders presents unique opportunities to access "undruggable" targets, but have often relied on stable 3D structures or structure-influenced latent spaces for effective binder generation. In this work, we introduce PepMLM, a target sequence-conditioned generator of de novo linear peptide binders. By employing a novel span masking strategy that uniquely positions cognate peptide sequences at the C-terminus of target protein sequences, PepMLM fine-tunes the state-of-the-art ESM-2 pLM to fully reconstruct the binder region, achieving low perplexities matching or improving upon validated peptide-protein sequence pairs. After successful in silico benchmarking with AlphaFold-Multimer, outperforming RFDiffusion on structured targets, we experimentally verify PepMLM's efficacy via fusion of model-derived peptides to E3 ubiquitin ligase domains, demonstrating endogenous degradation of emergent viral phosphoproteins and Huntington's disease-driving proteins. In total, PepMLM enables the generative design of candidate binders to any target protein, without the requirement of target structure, empowering downstream therapeutic applications.
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institution arXiv
publishDate 2023
record_format arxiv
spellingShingle PepMLM: Target Sequence-Conditioned Generation of Therapeutic Peptide Binders via Span Masked Language Modeling
Chen, Tianlai
Dumas, Madeleine
Watson, Rio
Vincoff, Sophia
Peng, Christina
Zhao, Lin
Hong, Lauren
Pertsemlidis, Sarah
Shaepers-Cheu, Mayumi
Wang, Tian Zi
Srijay, Divya
Monticello, Connor
Vure, Pranay
Pulugurta, Rishab
Kholina, Kseniia
Goel, Shrey
DeLisa, Matthew P.
Truant, Ray
Aguilar, Hector C.
Chatterjee, Pranam
Biomolecules
Target proteins that lack accessible binding pockets and conformational stability have posed increasing challenges for drug development. Induced proximity strategies, such as PROTACs and molecular glues, have thus gained attention as pharmacological alternatives, but still require small molecule docking at binding pockets for targeted protein degradation. The computational design of protein-based binders presents unique opportunities to access "undruggable" targets, but have often relied on stable 3D structures or structure-influenced latent spaces for effective binder generation. In this work, we introduce PepMLM, a target sequence-conditioned generator of de novo linear peptide binders. By employing a novel span masking strategy that uniquely positions cognate peptide sequences at the C-terminus of target protein sequences, PepMLM fine-tunes the state-of-the-art ESM-2 pLM to fully reconstruct the binder region, achieving low perplexities matching or improving upon validated peptide-protein sequence pairs. After successful in silico benchmarking with AlphaFold-Multimer, outperforming RFDiffusion on structured targets, we experimentally verify PepMLM's efficacy via fusion of model-derived peptides to E3 ubiquitin ligase domains, demonstrating endogenous degradation of emergent viral phosphoproteins and Huntington's disease-driving proteins. In total, PepMLM enables the generative design of candidate binders to any target protein, without the requirement of target structure, empowering downstream therapeutic applications.
title PepMLM: Target Sequence-Conditioned Generation of Therapeutic Peptide Binders via Span Masked Language Modeling
topic Biomolecules
url https://arxiv.org/abs/2310.03842