The Modified Combo i3+3 Design for Novel-Novel Combination Dose-Finding Trials in Oncology

Fuente: arXiv
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Autori principali: Liu, Jiaxin, Yuan, Shijie, Deng, Qiqi, Ji, Yuan
Natura: Preprint
Pubblicazione: 2024
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author Liu, Jiaxin
Yuan, Shijie
Deng, Qiqi
Ji, Yuan
author_facet Liu, Jiaxin
Yuan, Shijie
Deng, Qiqi
Ji, Yuan
contents We consider a modified Ci3+3 (MCi3+3) design for dual-agent dose-finding trials in which both agents are tested on multiple doses. This usually happens when the agents are novel therapies. The MCi3+3 design offers a two-stage or three-stage version, depending on the practical need. The first stage begins with single-agent dose escalation, the second stage launches a model-free combination dose finding for both agents, and optionally, the third stage follows with a model-based design. MCi3+3 aims to maintain a relatively simple framework to facilitate practical application, while also address challenges that are unique to novel-novel combination dose finding. Through simulations, we demonstrate that the MCi3+3 design adeptly manages various toxicity scenarios. It exhibits operational characteristics on par with other combination designs, while offering an enhanced safety profile. The design is motivated and tested for a real-life clinical trial.
format Preprint
id arxiv_https___arxiv_org_abs_2406_12666
institution arXiv
publishDate 2024
record_format arxiv
spellingShingle The Modified Combo i3+3 Design for Novel-Novel Combination Dose-Finding Trials in Oncology
Liu, Jiaxin
Yuan, Shijie
Deng, Qiqi
Ji, Yuan
Applications
We consider a modified Ci3+3 (MCi3+3) design for dual-agent dose-finding trials in which both agents are tested on multiple doses. This usually happens when the agents are novel therapies. The MCi3+3 design offers a two-stage or three-stage version, depending on the practical need. The first stage begins with single-agent dose escalation, the second stage launches a model-free combination dose finding for both agents, and optionally, the third stage follows with a model-based design. MCi3+3 aims to maintain a relatively simple framework to facilitate practical application, while also address challenges that are unique to novel-novel combination dose finding. Through simulations, we demonstrate that the MCi3+3 design adeptly manages various toxicity scenarios. It exhibits operational characteristics on par with other combination designs, while offering an enhanced safety profile. The design is motivated and tested for a real-life clinical trial.
title The Modified Combo i3+3 Design for Novel-Novel Combination Dose-Finding Trials in Oncology
topic Applications
url https://arxiv.org/abs/2406.12666