Covariate Adjustment in Randomized Experiments Motivated by Higher-Order Influence Functions

Fuente: arXiv
Saved in:
Bibliographic Details
Main Authors: Zhao, Sihui, Wang, Xinbo, Liu, Lin, Zhang, Xin
Format: Preprint
Published: 2024
Subjects:
Online Access:
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1866915624521826304
author Zhao, Sihui
Wang, Xinbo
Liu, Lin
Zhang, Xin
author_facet Zhao, Sihui
Wang, Xinbo
Liu, Lin
Zhang, Xin
contents Higher-Order Influence Functions (HOIF), developed in a series of papers over the past twenty years, are a fundamental theoretical device for constructing rate-optimal causal-effect estimators from observational studies. However, the value of HOIF for analyzing well-conducted randomized controlled trials (RCT) has not been explicitly explored. In the recent U.S. Food and Drug Administration and European Medicines Agency guidelines on the practice of covariate adjustment in analyzing RCT, in addition to the simple, unadjusted difference-in-mean estimator, it was also recommended to report the estimator adjusting for baseline covariates via a simple parametric working model, such as a linear model. However, when the number of baseline covariates $p$ is large, the recommendation is somewhat murky. In this paper, we show that HOIF-motivated estimators for the treatment-specific mean have significantly improved statistical properties compared to popular adjusted estimators in practice when $p$ is relatively large relative to the sample size $n$. We also characterize the conditions under which the HOIF-motivated estimator improves upon the unadjusted one. More importantly, we demonstrate that several state-of-the-art adjusted estimators proposed recently can be interpreted as particular HOIF-motivated estimators, thereby placing these estimators in a more unified framework. Numerical and empirical studies are conducted to corroborate our theoretical findings. An accompanying R package can be found on CRAN.
format Preprint
id arxiv_https___arxiv_org_abs_2411_08491
institution arXiv
publishDate 2024
record_format arxiv
spellingShingle Covariate Adjustment in Randomized Experiments Motivated by Higher-Order Influence Functions
Zhao, Sihui
Wang, Xinbo
Liu, Lin
Zhang, Xin
Methodology
Econometrics
Statistics Theory
Higher-Order Influence Functions (HOIF), developed in a series of papers over the past twenty years, are a fundamental theoretical device for constructing rate-optimal causal-effect estimators from observational studies. However, the value of HOIF for analyzing well-conducted randomized controlled trials (RCT) has not been explicitly explored. In the recent U.S. Food and Drug Administration and European Medicines Agency guidelines on the practice of covariate adjustment in analyzing RCT, in addition to the simple, unadjusted difference-in-mean estimator, it was also recommended to report the estimator adjusting for baseline covariates via a simple parametric working model, such as a linear model. However, when the number of baseline covariates $p$ is large, the recommendation is somewhat murky. In this paper, we show that HOIF-motivated estimators for the treatment-specific mean have significantly improved statistical properties compared to popular adjusted estimators in practice when $p$ is relatively large relative to the sample size $n$. We also characterize the conditions under which the HOIF-motivated estimator improves upon the unadjusted one. More importantly, we demonstrate that several state-of-the-art adjusted estimators proposed recently can be interpreted as particular HOIF-motivated estimators, thereby placing these estimators in a more unified framework. Numerical and empirical studies are conducted to corroborate our theoretical findings. An accompanying R package can be found on CRAN.
title Covariate Adjustment in Randomized Experiments Motivated by Higher-Order Influence Functions
topic Methodology
Econometrics
Statistics Theory
url https://arxiv.org/abs/2411.08491