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Main Authors: Chen, Cong, Huang, Mo
Format: Preprint
Published: 2025
Subjects:
Online Access:https://arxiv.org/abs/2502.16591
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author Chen, Cong
Huang, Mo
author_facet Chen, Cong
Huang, Mo
contents Adaptive Phase 2/3 designs hold great promise in contemporary oncology drug development, especially when limited data from Phase 1 dose-finding is insufficient for identifying an optimal dose. However, there is a general concern about inconsistent results before and after the adaptation. The imperfection in dose selection further complicates the issue. In this paper, we explicitly incorporate the concerns about inconsistency into the statistical analysis under three hypothesis testing strategies. This investigation paves the way for further research in a less explored area.
format Preprint
id arxiv_https___arxiv_org_abs_2502_16591
institution arXiv
publishDate 2025
record_format arxiv
spellingShingle Adjustment for Inconsistency in Adaptive Phase 2/3 Designs with Dose Optimization
Chen, Cong
Huang, Mo
Applications
Adaptive Phase 2/3 designs hold great promise in contemporary oncology drug development, especially when limited data from Phase 1 dose-finding is insufficient for identifying an optimal dose. However, there is a general concern about inconsistent results before and after the adaptation. The imperfection in dose selection further complicates the issue. In this paper, we explicitly incorporate the concerns about inconsistency into the statistical analysis under three hypothesis testing strategies. This investigation paves the way for further research in a less explored area.
title Adjustment for Inconsistency in Adaptive Phase 2/3 Designs with Dose Optimization
topic Applications
url https://arxiv.org/abs/2502.16591