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Main Authors: Li, Haoyang, Xu, Jie, Gan, Kyra, Wang, Fei, Zang, Chengxi
Format: Preprint
Published: 2025
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Online Access:https://arxiv.org/abs/2505.02238
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author Li, Haoyang
Xu, Jie
Gan, Kyra
Wang, Fei
Zang, Chengxi
author_facet Li, Haoyang
Xu, Jie
Gan, Kyra
Wang, Fei
Zang, Chengxi
contents Federated causal inference enables multi-site treatment effect estimation without sharing individual-level data, offering a privacy-preserving solution for real-world evidence generation. However, data heterogeneity across sites, manifested in differences in covariate, treatment, and outcome, poses significant challenges for unbiased and efficient estimation. In this paper, we present a comprehensive review and theoretical analysis of federated causal effect estimation across both binary/continuous and time-to-event outcomes. We classify existing methods into weight-based strategies and optimization-based frameworks and further discuss extensions including personalized models, peer-to-peer communication, and model decomposition. For time-to-event outcomes, we examine federated Cox and Aalen-Johansen models, deriving asymptotic bias and variance under heterogeneity. Our analysis reveals that FedProx-style regularization achieves near-optimal bias-variance trade-offs compared to naive averaging and meta-analysis. We review related software tools and conclude by outlining opportunities, challenges, and future directions for scalable, fair, and trustworthy federated causal inference in distributed healthcare systems.
format Preprint
id arxiv_https___arxiv_org_abs_2505_02238
institution arXiv
publishDate 2025
record_format arxiv
spellingShingle Federated Causal Inference in Healthcare: Methods, Challenges, and Applications
Li, Haoyang
Xu, Jie
Gan, Kyra
Wang, Fei
Zang, Chengxi
Machine Learning
Federated causal inference enables multi-site treatment effect estimation without sharing individual-level data, offering a privacy-preserving solution for real-world evidence generation. However, data heterogeneity across sites, manifested in differences in covariate, treatment, and outcome, poses significant challenges for unbiased and efficient estimation. In this paper, we present a comprehensive review and theoretical analysis of federated causal effect estimation across both binary/continuous and time-to-event outcomes. We classify existing methods into weight-based strategies and optimization-based frameworks and further discuss extensions including personalized models, peer-to-peer communication, and model decomposition. For time-to-event outcomes, we examine federated Cox and Aalen-Johansen models, deriving asymptotic bias and variance under heterogeneity. Our analysis reveals that FedProx-style regularization achieves near-optimal bias-variance trade-offs compared to naive averaging and meta-analysis. We review related software tools and conclude by outlining opportunities, challenges, and future directions for scalable, fair, and trustworthy federated causal inference in distributed healthcare systems.
title Federated Causal Inference in Healthcare: Methods, Challenges, and Applications
topic Machine Learning
url https://arxiv.org/abs/2505.02238