A Comparative Evaluation of Statistical Methods in Hybrid Controlled Trials
Fuente:
arXiv
Enregistré dans:
| Auteurs principaux: | Ran, Di, Zhang, Fanni, Shahsavari, Sima, Broglio, Kristine, Henderson, Alasdair, Yu, Binbing |
|---|---|
| Format: | Preprint |
| Publié: |
2025
|
| Sujets: | |
| Accès en ligne: | |
| Tags: |
Ajouter un tag
Pas de tags, Soyez le premier à ajouter un tag!
|
Documents similaires
CUI-MET: Clinical Utility Index Dose Optimization Approach for Multiple-Dose, Multiple-Outcome Randomized Trial Designs
par: Zhang, Fanni, et autres
Publié: (2025)
par: Zhang, Fanni, et autres
Publié: (2025)
Enhancing Statistical Validity and Power in Hybrid Controlled Trials: A Randomization Inference Approach with Conformal Selective Borrowing
par: Zhu, Ke, et autres
Publié: (2024)
par: Zhu, Ke, et autres
Publié: (2024)
Utility-Based Dose Optimization Approaches for Multiple-Dose Randomized Trial Designs Accounting for Multiple Endpoints
par: DAngelo, Gina, et autres
Publié: (2025)
par: DAngelo, Gina, et autres
Publié: (2025)
Selection Bias in Hybrid Randomized Controlled Trials using External Controls: A Simulation Study
par: Chiam, Han Chang, et autres
Publié: (2025)
par: Chiam, Han Chang, et autres
Publié: (2025)
A Non-Parametric Sensitivity Analysis for Bounding Bias in Hybrid Control Trials
par: Gordon, Alissa, et autres
Publié: (2025)
par: Gordon, Alissa, et autres
Publié: (2025)
BMW: Bayesian Model-Assisted Adaptive Phase II Clinical Trial Design for Win Ratio Statistic
par: Zhu, Di, et autres
Publié: (2026)
par: Zhu, Di, et autres
Publié: (2026)
Designing Efficient Hybrid and Single-Arm Trials: External Control Borrowing and Sample Size Calculation
par: Gao, Yujing, et autres
Publié: (2025)
par: Gao, Yujing, et autres
Publié: (2025)
A Model-Robust G-Computation Method for Analyzing Hybrid Control Studies Without Assuming Exchangeability
par: Zhang, Zhiwei, et autres
Publié: (2026)
par: Zhang, Zhiwei, et autres
Publié: (2026)
Outcome Regression Methods for Analyzing Hybrid Control Studies: Balancing Bias and Variability
par: Zhang, Zhiwei, et autres
Publié: (2025)
par: Zhang, Zhiwei, et autres
Publié: (2025)
Evaluating and Testing for Actionable Treatment Effect Heterogeneity
par: Ashouri, Mahsa, et autres
Publié: (2025)
par: Ashouri, Mahsa, et autres
Publié: (2025)
A General Framework for Designing and Evaluating Active-Controlled Trials with Non-Inferiority Objectives
par: Olivas-Martinez, Antonio, et autres
Publié: (2025)
par: Olivas-Martinez, Antonio, et autres
Publié: (2025)
A Comparative Evaluation of Bayesian Model-Assisted Two-Stage Designs for Phase I/II Clinical Trials
par: Sun, Hao, et autres
Publié: (2025)
par: Sun, Hao, et autres
Publié: (2025)
Robust Estimation and Inference in Hybrid Controlled Trials for Binary Outcomes: A Case Study on Non-Small Cell Lung Cancer
par: Liu, Jiajun, et autres
Publié: (2025)
par: Liu, Jiajun, et autres
Publié: (2025)
Statistical Design and Planning of an Adaptive Trial using Hierarchical Composite Outcomes: A Practical example
par: Padmanabhan, Krishna, et autres
Publié: (2025)
par: Padmanabhan, Krishna, et autres
Publié: (2025)
Who's Winning? Clarifying Estimands Based on Win Statistics in Cluster Randomized Trials
par: Lee, Kenneth M., et autres
Publié: (2026)
par: Lee, Kenneth M., et autres
Publié: (2026)
Augmented Binary Method for Basket Trials (ABBA)
par: Cherlin, Svetlana, et autres
Publié: (2024)
par: Cherlin, Svetlana, et autres
Publié: (2024)
Active-Controlled Trial Design for HIV Prevention Trials with a Counterfactual Placebo
par: Gao, Fei, et autres
Publié: (2024)
par: Gao, Fei, et autres
Publié: (2024)
Evaluation of optimal cut-offs and dichotomous combinations for two biomarkers to improve patient selection
par: DAngelo, Gina, et autres
Publié: (2025)
par: DAngelo, Gina, et autres
Publié: (2025)
A Practical Guide to Interpret a Randomized Controlled Trial
par: Tanboga, Ibrahim Halil
Publié: (2026)
par: Tanboga, Ibrahim Halil
Publié: (2026)
Novel Methods for the Analysis of Stepped Wedge Cluster Randomized Trials
par: Kennedy-Shaffer, Lee, et autres
Publié: (2019)
par: Kennedy-Shaffer, Lee, et autres
Publié: (2019)
Comparing HIV Vaccine Immunogenicity across Trials with Different Populations and Study Designs
par: Jin, Yutong, et autres
Publié: (2024)
par: Jin, Yutong, et autres
Publié: (2024)
Synthetic Control Method with Mixed Frequency Data
par: Zhang, Lu, et autres
Publié: (2026)
par: Zhang, Lu, et autres
Publié: (2026)
Evaluating Informative Cluster Size in Cluster Randomized Trials
par: Blette, Bryan S., et autres
Publié: (2025)
par: Blette, Bryan S., et autres
Publié: (2025)
Robust Updating of a Risk Prediction Model by Integrating External Ranking Information
par: Henderson, Nicholas C.
Publié: (2026)
par: Henderson, Nicholas C.
Publié: (2026)
Evaluating LLMs When They Do Not Know the Answer: Statistical Evaluation of Mathematical Reasoning via Comparative Signals
par: Dong, Zihan, et autres
Publié: (2026)
par: Dong, Zihan, et autres
Publié: (2026)
An Integrated and Coherent Framework for Point Estimation and Hypothesis Testing with Concurrent Controls in Platform Trials
par: Zhan, Tianyu, et autres
Publié: (2025)
par: Zhan, Tianyu, et autres
Publié: (2025)
A Hybrid Framework Combining Autoregression and Common Factors for Matrix Time Series
par: Fan, Zhiyun, et autres
Publié: (2025)
par: Fan, Zhiyun, et autres
Publié: (2025)
Guarantees for Comprehensive Simulation Assessment of Statistical Methods
par: Yang, James, et autres
Publié: (2022)
par: Yang, James, et autres
Publié: (2022)
A Workflow for Evaluating Regional Treatment Effect Heterogeneity in Multi-Regional Clinical Trials
par: Zhang, Cong, et autres
Publié: (2026)
par: Zhang, Cong, et autres
Publié: (2026)
Proximal Learning for Trials With External Controls: A Case Study in HIV Prevention
par: Song, Yilin, et autres
Publié: (2026)
par: Song, Yilin, et autres
Publié: (2026)
Building a Standardised Statistical Reporting Toolbox in an Academic Oncology Clinical Trials Unit: The grstat R Package
par: Chaltiel, Dan, et autres
Publié: (2026)
par: Chaltiel, Dan, et autres
Publié: (2026)
Asymptotic Online FWER Control for Dependent Test Statistics
par: Jankovic, Vincent, et autres
Publié: (2024)
par: Jankovic, Vincent, et autres
Publié: (2024)
Leveraging External Controls in Clinical Trials: Estimands, Estimation, Assumptions
par: Liu, Bo, et autres
Publié: (2025)
par: Liu, Bo, et autres
Publié: (2025)
COADVISE: Covariate Adjustment with Variable Selection in Randomized Controlled Trials
par: Liu, Yi, et autres
Publié: (2025)
par: Liu, Yi, et autres
Publié: (2025)
Causal Survival Analysis in Platform Trials with Non-Concurrent Controls
par: D'Alessandro, Antonio, et autres
Publié: (2026)
par: D'Alessandro, Antonio, et autres
Publié: (2026)
Notes on Randomized Controlled Trials for Studying Social Media Harms
par: Felton, Chris
Publié: (2026)
par: Felton, Chris
Publié: (2026)
A Review of Statistical Methods for Handling Nonignorable Missing Data using Instrument Approach
par: Zhao, Yujie
Publié: (2025)
par: Zhao, Yujie
Publié: (2025)
Integrating Randomized Controlled Trial and External Control Data Using Balancing Weights: A Comparison of Estimands and Estimators
par: Wang, Peijin, et autres
Publié: (2025)
par: Wang, Peijin, et autres
Publié: (2025)
Externally Controlled Trials: A Review of Design and Borrowing Through a Causal Lens
par: Zhu, Ke, et autres
Publié: (2026)
par: Zhu, Ke, et autres
Publié: (2026)
A Review of Methods and Practices for Missing Data in Sequential Multiple Assignment Randomized Trials (SMARTs): An Ancillary Study of a Scoping Review
par: Freeman, Nikki L. B., et autres
Publié: (2026)
par: Freeman, Nikki L. B., et autres
Publié: (2026)
Documents similaires
-
CUI-MET: Clinical Utility Index Dose Optimization Approach for Multiple-Dose, Multiple-Outcome Randomized Trial Designs
par: Zhang, Fanni, et autres
Publié: (2025) -
Enhancing Statistical Validity and Power in Hybrid Controlled Trials: A Randomization Inference Approach with Conformal Selective Borrowing
par: Zhu, Ke, et autres
Publié: (2024) -
Utility-Based Dose Optimization Approaches for Multiple-Dose Randomized Trial Designs Accounting for Multiple Endpoints
par: DAngelo, Gina, et autres
Publié: (2025) -
Selection Bias in Hybrid Randomized Controlled Trials using External Controls: A Simulation Study
par: Chiam, Han Chang, et autres
Publié: (2025) -
A Non-Parametric Sensitivity Analysis for Bounding Bias in Hybrid Control Trials
par: Gordon, Alissa, et autres
Publié: (2025)