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author Fang, Zhangyun
Zhan, Shuai
Mao, Churu
Zhang, Ningjing
Zhao, Xiaofeng
Huang, Yun
Ding, Wanjing
Ma, Zhongjun
author_facet Fang, Zhangyun
Zhan, Shuai
Mao, Churu
Zhang, Ningjing
Zhao, Xiaofeng
Huang, Yun
Ding, Wanjing
Ma, Zhongjun
Fang, Zhangyun
Zhan, Shuai
Mao, Churu
Zhang, Ningjing
Zhao, Xiaofeng
Huang, Yun
Ding, Wanjing
Ma, Zhongjun
collection PubMed - marine biology
contents Discovery of an orally bioavailable pyridone-based BRD4 inhibitor with potent antitumor efficacy in colorectal cancer. Fang, Zhangyun Zhan, Shuai Mao, Churu Zhang, Ningjing Zhao, Xiaofeng Huang, Yun Ding, Wanjing Ma, Zhongjun Bromodomain Containing Proteins Humans Animals Cell Cycle Proteins Antineoplastic Agents Colorectal Neoplasms Transcription Factors Mice Administration, Oral Cell Proliferation Structure-Activity Relationship Drug Discovery Pyridones Drug Screening Assays, Antitumor Dose-Response Relationship, Drug Molecular Structure Biological Availability Mice, Nude Neoplasms, Experimental Colorectal cancer (CRC) remains a major clinical burden with limited durable responses. Given reports implicating Bromodomain-containing protein 4 (BRD4) in CRC proliferation and therapy resistance, more potent BRD4-targeting agents with proven in-vivo activity are needed. Through virtual screening followed by structure-guided chemical modification, we identified H5 as a BRD4 inhibitor. In biochemical assays, H5 shows IC = 7.9 ± 0.5 nM, outperforming JQ-1 (IC = 33.0 ± 1.0 nM) by 4-fold. Molecular dynamics simulations indicate that H5 engages BRD4 via hydrogen bonds with Asn140 and Asp88 and a water-mediated bridge to Gln85. In the HCT-116 xenograft mouse model, oral administration of H5 suppressed tumor growth (TGI = 82 % at 50 mg/kg) and downregulated the BRD4-driven oncoproteins c-MYC and BCL-2. Collectively, H5 emerges as a highly promising BRD4-targeted candidate for colorectal cancer treatment.
format Artículo científico
id pubmed_41544579
institution PubMed
language en
publishDate 2026
publisher European journal of medicinal chemistry
record_format pubmed
spellingShingle Discovery of an orally bioavailable pyridone-based BRD4 inhibitor with potent antitumor efficacy in colorectal cancer.
Fang, Zhangyun
Zhan, Shuai
Mao, Churu
Zhang, Ningjing
Zhao, Xiaofeng
Huang, Yun
Ding, Wanjing
Ma, Zhongjun
Bromodomain Containing Proteins
Humans
Animals
Cell Cycle Proteins
Antineoplastic Agents
Colorectal Neoplasms
Transcription Factors
Mice
Administration, Oral
Cell Proliferation
Structure-Activity Relationship
Drug Discovery
Pyridones
Drug Screening Assays, Antitumor
Dose-Response Relationship, Drug
Molecular Structure
Biological Availability
Mice, Nude
Neoplasms, Experimental
Discovery of an orally bioavailable pyridone-based BRD4 inhibitor with potent antitumor efficacy in colorectal cancer. Fang, Zhangyun Zhan, Shuai Mao, Churu Zhang, Ningjing Zhao, Xiaofeng Huang, Yun Ding, Wanjing Ma, Zhongjun Bromodomain Containing Proteins Humans Animals Cell Cycle Proteins Antineoplastic Agents Colorectal Neoplasms Transcription Factors Mice Administration, Oral Cell Proliferation Structure-Activity Relationship Drug Discovery Pyridones Drug Screening Assays, Antitumor Dose-Response Relationship, Drug Molecular Structure Biological Availability Mice, Nude Neoplasms, Experimental Colorectal cancer (CRC) remains a major clinical burden with limited durable responses. Given reports implicating Bromodomain-containing protein 4 (BRD4) in CRC proliferation and therapy resistance, more potent BRD4-targeting agents with proven in-vivo activity are needed. Through virtual screening followed by structure-guided chemical modification, we identified H5 as a BRD4 inhibitor. In biochemical assays, H5 shows IC = 7.9 ± 0.5 nM, outperforming JQ-1 (IC = 33.0 ± 1.0 nM) by 4-fold. Molecular dynamics simulations indicate that H5 engages BRD4 via hydrogen bonds with Asn140 and Asp88 and a water-mediated bridge to Gln85. In the HCT-116 xenograft mouse model, oral administration of H5 suppressed tumor growth (TGI = 82 % at 50 mg/kg) and downregulated the BRD4-driven oncoproteins c-MYC and BCL-2. Collectively, H5 emerges as a highly promising BRD4-targeted candidate for colorectal cancer treatment.
title Discovery of an orally bioavailable pyridone-based BRD4 inhibitor with potent antitumor efficacy in colorectal cancer.
topic Bromodomain Containing Proteins
Humans
Animals
Cell Cycle Proteins
Antineoplastic Agents
Colorectal Neoplasms
Transcription Factors
Mice
Administration, Oral
Cell Proliferation
Structure-Activity Relationship
Drug Discovery
Pyridones
Drug Screening Assays, Antitumor
Dose-Response Relationship, Drug
Molecular Structure
Biological Availability
Mice, Nude
Neoplasms, Experimental
url https://pubmed.ncbi.nlm.nih.gov/41544579/