Onasemnogene‐abeparvovec administration to premature infants with spinal muscular atrophy
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Wiley Open Access
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| Main Authors: | Stephen M. Brown, Aparna S. Ajjarapu, Divya Ramachandra, Laura Blasco‐Pérez, Mar Costa‐Roger, Eduardo F. Tizzano, Charlotte J. Sumner, Katherine D. Mathews |
|---|---|
| Format: | Artículo Open Access |
| Published: |
Wiley
2024
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