AAV9‐ DARS2 Gene Therapy Rescues Phenotype in Leukoencephalopathy with Brainstem and Spinal Cord Involvement and Lactate Elevation Patient Cells and Neuronal Dars2 Deficient Mice

Fuente: Wiley Open Access
Saved in:
Bibliographic Details
Main Authors: I Garofolo, B Lindsay, Y Liang, B Ratajczak, M Janowski, P Walczak, A Fatemi, CL Nemeth
Format: Artículo Open Access
Published: Wiley 2025
Subjects:
Online Access:
Tags: Add Tag
No Tags, Be the first to tag this record!