Extended long‐term efficacy and safety of velmanase alfa treatment up to 12 years in patients with alpha‐mannosidosis

Fuente: Wiley Open Access
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Bibliographic Details
Main Authors: Nathalie Guffon, Line Borgwardt, Anna Tylki‐Szymańska, Andrea Ballabeni, Francesca Donà, Amer Joseph, Henriët Nienhuis, Caterina Maugeri, Allan Lund
Format: Artículo Open Access
Published: Wiley 2024
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