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  • Long‐Term Outcomes of Chenodeoxycholic Acid Therapy for Cerebrotendinous Xanthomatosis: A Nationwide Study on Prognostic Factors and Treatment Response
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Long‐Term Outcomes of Chenodeoxycholic Acid Therapy for Cerebrotendinous Xanthomatosis: A Nationwide Study on Prognostic Factors and Treatment Response

Fuente: Wiley Open Access
Salvato in:
Dettagli Bibliografici
Autori principali: Tanyel Zubarioglu, Banu Kadıoğlu‐Yılmaz, Engin Köse, Pelin Teke‐Kısa, Mehmet Cihan Balcı, Havva Yazıcı, Burcu Özturk‐Hişmi, Abdurrahman Akgün, Deniz Kor, Sevil Yıldız, Gonca Kılıç‐Yıldırım, Erdoğan Soyuçen, Aylin Akçalı, Yılmaz Yıldız, Aslı Durmuş, Dilek Güneş, Pembe Soylu‐Üstkoyuncu, Çiğdem Seher Kasapkara, Şahin Erdöl, Emine Göksoy, Halil Tuna Akar, Haluk Gümüş, Ahmet Hakan Ekmekçi, Fatma Tuba Eminoğlu, Nur Arslan, Haşmet Ayhan Hanağası, Ebru Canda, Emine Genç, Işıl Özer, Ayşegül Gündüz, Ertuğrul Kıykım, Çiğdem Aktuğlu‐Zeybek
Natura: Artículo Open Access
Pubblicazione: Wiley 2025
Soggetti:
Journal of Inherited Metabolic Disease
Accesso online:
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DOI:10.1002/jimd.70069

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