Female Patients With Mucopolysaccharidosis II ( MPS II ): Insights From the Hunter Outcome Survey

Fuente: Wiley Open Access
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Bibliographic Details
Main Authors: Barbara K. Burton, Hernan Amartino, Roberto Giugliani, Christoph Kampmann, Julian Raiman, Maurizio Scarpa, Anna Tylki‐Szymańska, Jennifer Audi, Jaco Botha, Siddarth Jain, Joseph Muenzer
Format: Artículo Open Access
Published: Wiley 2025
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