Risdiplam Add‐On Therapy Following Onasemnogene Abeparvovec in Children With Spinal Muscular Atrophy and 2 SMN2 Copies: A Multi‐Center Case Series

Fuente: Wiley Open Access
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Bibliographic Details
Main Authors: Corinna Stoltenburg, Klaus Goldhahn, Arpad von Moers, Angela M. Kaindl, Claudia Weiß
Format: Artículo Open Access
Published: Wiley 2026
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