Pre‐symptomatic risdiplam treatment for spinal muscular atrophy initiated at 12 days post‐birth: 14‐month safety and developmental outcomes

Fuente: Wiley Open Access
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Bibliographic Details
Main Authors: Zhihao Sun, Liping Wu, Yufan Hui, Yuhang Zhong, Jiangtao Yang, Zhiyong Sun, Xiaoling Huang, Hui Xiong
Format: Artículo Open Access
Published: Wiley 2025
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