A Pharmacometrics‐Informed Trial Simulation Framework for Optimizing Study Designs for Disease‐Modifying Treatments in Rare Neurological Disorders

Fuente: Wiley Open Access
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Bibliographic Details
Main Authors: Yevgen Ryeznik, Ralf‐Dieter Hilgers, Nicole Heussen, Emmanuelle Comets, France Mentré, Niels Hendrickx, Mats O. Karlsson, Andrew C. Hooker, Alzahra Hamdan, Xiaomei Chen, Rebecca Schüle, Matthis Synofzik, Oleksandr Sverdlov
Format: Artículo Open Access
Published: Wiley 2025
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