WATCH: A Workflow to Assess Treatment Effect Heterogeneity in Drug Development for Clinical Trial Sponsors
Fuente:
Wiley Open Access
Enregistré dans:
| Auteurs principaux: | Konstantinos Sechidis, Sophie Sun, Yao Chen, Jiarui Lu, Cong Zhang, Mark Baillie, David Ohlssen, Marc Vandemeulebroecke, Rob Hemmings, Stephen Ruberg, Björn Bornkamp |
|---|---|
| Format: | Artículo Open Access |
| Publié: |
Wiley
2024
|
| Sujets: | |
| Accès en ligne: | |
| Tags: |
Ajouter un tag
Pas de tags, Soyez le premier à ajouter un tag!
|
Documents similaires
WATCH: A Workflow to Assess Treatment Effect Heterogeneity in Drug Development for Clinical Trial Sponsors
par: Sechidis, Konstantinos, et autres
Publié: (2024)
par: Sechidis, Konstantinos, et autres
Publié: (2024)
Predicting subgroup treatment effects for a new study: Motivations, results and learnings from running a data challenge in a pharmaceutical corporation
par: Björn Bornkamp, et autres
Publié: (2024)
par: Björn Bornkamp, et autres
Publié: (2024)
Detection of Outlying Correlation Coefficients in Multicenter Clinical Trials
par: Lieven Desmet, et autres
Publié: (2025)
par: Lieven Desmet, et autres
Publié: (2025)
A case study: Assessing the efficacy of the revised dosage regimen via prediction model for recurrent event rate using biomarker data
par: Ahrim Youn, et autres
Publié: (2024)
par: Ahrim Youn, et autres
Publié: (2024)
Principles for Defining Estimands in Clinical Trials—A Proposal
par: Tobias Mütze, et autres
Publié: (2024)
par: Tobias Mütze, et autres
Publié: (2024)
CUSUMIN Combination: A Cumulative Sum Interval Design for Phase I Cancer Drug‐Combination Trials
par: Tomoyoshi Hatayama, et autres
Publié: (2025)
par: Tomoyoshi Hatayama, et autres
Publié: (2025)
Do You Want to Stay Single? Considerations on Single‐Arm Trials in Drug Development and the Postregulatory Space
par: Yulia Dyachkova, et autres
Publié: (2024)
par: Yulia Dyachkova, et autres
Publié: (2024)
Great Wall: A Generalized Dose Optimization Design for Drug Combination Trials Maximizing Survival Benefit
par: Yan Han, et autres
Publié: (2025)
par: Yan Han, et autres
Publié: (2025)
A Unified Approach to Covariate Adjustment for Survival Endpoints in Randomized Clinical Trials
par: Zhiwei Zhang, et autres
Publié: (2025)
par: Zhiwei Zhang, et autres
Publié: (2025)
Designing and Evaluating Bayesian Advanced Adaptive Randomised Clinical Trials: A Practical Guide
par: Anders Granholm, et autres
Publié: (2025)
par: Anders Granholm, et autres
Publié: (2025)
Bayesian Response Adaptive Randomization for Randomized Clinical Trials With Continuous Outcomes: The Role of Covariate Adjustment
par: Vahan Aslanyan, et autres
Publié: (2024)
par: Vahan Aslanyan, et autres
Publié: (2024)
Mediation Analysis of Path‐Specific Effects in Randomised Clinical Trials With Repeatedly Measured Mediators and Outcomes
par: Martin Linder, et autres
Publié: (2025)
par: Martin Linder, et autres
Publié: (2025)
Drift Parameter Based Sample Size Determination in Multi‐Stage Bayesian Randomized Clinical Trials
par: Yueyang Han, et autres
Publié: (2025)
par: Yueyang Han, et autres
Publié: (2025)
Bayesian Power‐Based Sample Size Determination for Single‐Arm Clinical Trials With Time‐to‐Event Endpoints
par: Go Horiguchi, et autres
Publié: (2026)
par: Go Horiguchi, et autres
Publié: (2026)
Why “Minimal Clinically Important Difference” for Interpreting the Magnitude of the Treatment Effect Is Not Useful
par: Jitendra Ganju
Publié: (2025)
par: Jitendra Ganju
Publié: (2025)
Using Individualized Treatment Effects to Assess Treatment Effect Heterogeneity
par: Sechidis, Konstantinos, et autres
Publié: (2025)
par: Sechidis, Konstantinos, et autres
Publié: (2025)
Using Individualized Treatment Effects to Assess Treatment Effect Heterogeneity
par: Konstantinos Sechidis, et autres
Publié: (2025)
par: Konstantinos Sechidis, et autres
Publié: (2025)
A Bayesian Dynamic Model‐Based Adaptive Design for Oncology Dose Optimization in Phase I/II Clinical Trials
par: Yingjie Qiu, et autres
Publié: (2024)
par: Yingjie Qiu, et autres
Publié: (2024)
Control of Unconditional Type I Error in Clinical Trials With External Control Borrowing—A Two‐Stage Adaptive Design Perspective
par: Ping Gao, et autres
Publié: (2025)
par: Ping Gao, et autres
Publié: (2025)
Simulation‐Based Bayesian Predictive Probability of Success for Interim Monitoring of Clinical Trials With Competing Event Data: Two Case Studies
par: Chiara Micoli, et autres
Publié: (2025)
par: Chiara Micoli, et autres
Publié: (2025)
A Statistical Concept for Conditional Marketing Authorisation Based on the Intermediate and Final Outcomes of a Single Confirmatory Randomised Clinical Trial
par: Xiaofei Liu, et autres
Publié: (2026)
par: Xiaofei Liu, et autres
Publié: (2026)
بیوتکنولوژی دارویی | اصول و کاربردها
par: Qalavand, Mostafa
Publié: (2025)
par: Qalavand, Mostafa
Publié: (2025)
A Tree‐Based Scan Statistic for Detecting Signals of Drug–Drug Interactions in Spontaneous Reporting Databases
par: Seok‐Jae Heo, et autres
Publié: (2025)
par: Seok‐Jae Heo, et autres
Publié: (2025)
Pre‐Posterior Distributions in Drug Development and Their Properties
par: Andrew P. Grieve
Publié: (2024)
par: Andrew P. Grieve
Publié: (2024)
Applying the Estimand Framework to Non‐Inferiority Trials
par: Helle Lynggaard, et autres
Publié: (2024)
par: Helle Lynggaard, et autres
Publié: (2024)
Personalized Treatment Selection for Multivariate Ordinal Scale Outcomes and Multiple Treatments
par: Chathura Siriwardhana, et autres
Publié: (2025)
par: Chathura Siriwardhana, et autres
Publié: (2025)
Variable Duration Trial as an Alternative Design for Continuous Endpoints
par: Jitendra Ganju, et autres
Publié: (2024)
par: Jitendra Ganju, et autres
Publié: (2024)
Global Pharmaceutical Container Market 2025 To 2034
par: Sirsat, Nitin
Publié: (2025)
par: Sirsat, Nitin
Publié: (2025)
Estimation of Treatment Policy Estimands for Continuous Outcomes Using Off‐Treatment Sequential Multiple Imputation
par: Thomas Drury, et autres
Publié: (2024)
par: Thomas Drury, et autres
Publié: (2024)
Applying the Principal Stratum Strategy in Equivalence Trials: A Case Study
par: Jerome Sepin, et autres
Publié: (2025)
par: Jerome Sepin, et autres
Publié: (2025)
“Within‐Trial” Prognostic Score Adjustment Is Targeted Maximum Likelihood Estimation
par: Emilie Højbjerre‐Frandsen, et autres
Publié: (2026)
par: Emilie Højbjerre‐Frandsen, et autres
Publié: (2026)
Comparing Methods to Assess Treatment Effect Heterogeneity in General Parametric Regression Models
par: Yao Chen, et autres
Publié: (2026)
par: Yao Chen, et autres
Publié: (2026)
Bayesian Solutions for Assessing Differential Effects in Biomarker Positive and Negative Subgroups
par: Dan Jackson, et autres
Publié: (2024)
par: Dan Jackson, et autres
Publié: (2024)
Using Off‐Treatment Sequential Multiple Imputation for Binary Outcomes to Address Intercurrent Events Handled by a Treatment Policy Strategy
par: Sunita Rehal, et autres
Publié: (2026)
par: Sunita Rehal, et autres
Publié: (2026)
Machine Learning Approaches for Accelerating Drug Discovery and Reducing Clinical Trial Failures.
par: Sudhir, Siddharth
Publié: (2025)
par: Sudhir, Siddharth
Publié: (2025)
Utility‐Based Dose Optimization Approaches for Multiple‐Dose Randomized Trial Designs Accounting for Multiple Endpoints
par: Gina D'Angelo, et autres
Publié: (2025)
par: Gina D'Angelo, et autres
Publié: (2025)
Assessing the Operational Characteristics of the Individual Causal Association as a Metric of Surrogacy in the Binary Continuous Setting
par: Fenny Ong, et autres
Publié: (2024)
par: Fenny Ong, et autres
Publié: (2024)
A Model‐Based Trial Design With a Randomization Scheme Considering Pharmacokinetics Exposure for Dose Optimization in Oncology
par: Jun Zhang, et autres
Publié: (2024)
par: Jun Zhang, et autres
Publié: (2024)
Informing the Borrowing Process for Dose‐Finding Trials by Estimating the Similarity Between Population‐Specific Dose‐Toxicity Curves
par: Dario Zocholl, et autres
Publié: (2025)
par: Dario Zocholl, et autres
Publié: (2025)
Approximate Bayesian Analysis for Borrowing External Controls for Randomized Controlled Trials With Dynamic Borrowing and Covariate Balancing Adjustment
par: Jixian Wang, et autres
Publié: (2025)
par: Jixian Wang, et autres
Publié: (2025)
Documents similaires
-
WATCH: A Workflow to Assess Treatment Effect Heterogeneity in Drug Development for Clinical Trial Sponsors
par: Sechidis, Konstantinos, et autres
Publié: (2024) -
Predicting subgroup treatment effects for a new study: Motivations, results and learnings from running a data challenge in a pharmaceutical corporation
par: Björn Bornkamp, et autres
Publié: (2024) -
Detection of Outlying Correlation Coefficients in Multicenter Clinical Trials
par: Lieven Desmet, et autres
Publié: (2025) -
A case study: Assessing the efficacy of the revised dosage regimen via prediction model for recurrent event rate using biomarker data
par: Ahrim Youn, et autres
Publié: (2024) -
Principles for Defining Estimands in Clinical Trials—A Proposal
par: Tobias Mütze, et autres
Publié: (2024)