Long‐term assessment of haematological recovery following somatic genetic rescue in a MYSM1‐deficient patient: Implications for in vivo gene therapy

Fuente: Wiley Open Access
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Bibliographic Details
Main Authors: Sophie de Tocqueville, Emmanuel Martin, Quentin Riller, Laëtitia Kermasson, Benoit France, Aude Magérus, Frédéric Rieux‐Laucat, François Delhommeau, Pierre Hirsch, Aurore Touzart, Aude Echalier, Alain Fischer, Despina Moshous, Patrick Revy
Format: Artículo Open Access
Published: Wiley 2024
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