Start, switch and stop (triple‐S) criteria for enzyme replacement therapy of late‐onset Pompe disease: European Pompe Consortium recommendation update 2024

Fuente: Wiley Open Access
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Bibliographic Details
Main Authors: Benedikt Schoser, Nadine A. M. E. van der Beek, Alexander Broomfield, Esther Brusse, Jordi Diaz‐Manera, Andreas Hahn, Thomas Hundsberger, Cornelia Kornblum, Michelle Kruijshaar, Pascal Laforet, Eugen Mengel, Tiziana Mongini, David Orlikowski, Giancarlo Parenti, W. W. M. Pim Pijnappel, Mark Roberts, Thomas Scherer, Antonio Toscano, John Vissing, Johanna M. P. van den Hout, Pieter A. van Doorn, Stephan Wenninger, Ans T. van der Ploeg
Format: Artículo Open Access
Published: Wiley 2024
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