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AI-designed, fully in silico mRNA enzyme replacement therapy for Hunter Syndrome.

Fuente: Zenodo

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Bibliographic Details
Main Author:	Alkhaleeli, Rami
Format:	Recurso digital
Language:	English
Published:	Zenodo 2025
Subjects:	Hunter Syndrome MPS II Iduronate-2-sulfatase (IDS) mRNA therapeutics AI-guided drug design Computational biology Codon optimization RNA secondary structure Immunogenicity prediction LNP delivery modeling Rare disease therapeutics Lysosomal storage disorders Enzyme replacement therapy In silico modeling Pharmacoeconomic analysis
Online Access:	Acceder al recurso
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