Transcriptomic Analysis in Autism Spectrum Disorder Suggests Three Molecular Subtypes with Distinct Phenotypic Profiles and Functional Pathways

Fuente: Zenodo
Gespeichert in:
Bibliographische Detailangaben
1. Verfasser: Tao
Format: Recurso digital
Veröffentlicht: Zenodo 2026
Online-Zugang:
Tags: Tag hinzufügen
Keine Tags, Fügen Sie den ersten Tag hinzu!
_version_ 1866902337084194816
author Tao
author_facet Tao
contents <p><strong><span lang="EN-US">Background</span></strong></p> <p><span lang="EN-US">Autism spectrum disorder (ASD) is highly heterogeneous. Molecular subtyping of ASD based on gene expression data will help address the biological heterogeneity of ASD. </span></p> <p><strong><span lang="EN-US">Methods</span></strong></p> <p><span lang="EN-US">We analyzed RNA-seq data from 1,711 ASD samples, employing unsupervised non-negative matrix factorization (NMF) to identify subtypes, and characterized them with five categories: overall ASD symptoms, social-communication deficits, restricted-repetitive-stereotyped behaviors, cognitive-adaptive function and behavior problems. We also explored subtype-specific differentially expressed genes, functional pathways, and spatiotemporal/cell-type characteristics.</span></p> <p><strong><span lang="EN-US">Results</span></strong></p> <p><span lang="EN-US">NMF analysis identified three ASD subtypes. The three subtypes exhibited different phenotypic patterns: Cluster 1 had severe restricted and repetitive behaviors, Cluster 3 mainly had social communication impairments, Cluster 2 presented milder symptoms and better cognitive function. Differential expressed genes analysis linked Cluster 1 and Cluster3 to nervous system dysfunctions and morphogenesis of a branching structure, while Cluster 2 to immune system processes. The clusters also exhibited distinct gene expression patterns across brain regions, developmental stages, and cell types. Validation in two independent datasets confirmed the reproducibility of the distinct clusters.<strong> </strong></span></p> <p><strong><span lang="EN-US">Conclusions</span></strong></p> <p><span lang="EN-US">This molecular subtyping reveals biologically and clinically distinct subtypes of ASD, helping to understand the atypical mechanisms underlying ASD heterogeneity. It also contributes to the development of personalized therapeutic strategies for distinct subtypes. <span> </span></span></p>
format Recurso digital
id zenodo_https___doi_org_10_5281_zenodo_19124179
institution Zenodo
language
publishDate 2026
publisher Zenodo
record_format zenodo
spellingShingle Transcriptomic Analysis in Autism Spectrum Disorder Suggests Three Molecular Subtypes with Distinct Phenotypic Profiles and Functional Pathways
Tao
<p><strong><span lang="EN-US">Background</span></strong></p> <p><span lang="EN-US">Autism spectrum disorder (ASD) is highly heterogeneous. Molecular subtyping of ASD based on gene expression data will help address the biological heterogeneity of ASD. </span></p> <p><strong><span lang="EN-US">Methods</span></strong></p> <p><span lang="EN-US">We analyzed RNA-seq data from 1,711 ASD samples, employing unsupervised non-negative matrix factorization (NMF) to identify subtypes, and characterized them with five categories: overall ASD symptoms, social-communication deficits, restricted-repetitive-stereotyped behaviors, cognitive-adaptive function and behavior problems. We also explored subtype-specific differentially expressed genes, functional pathways, and spatiotemporal/cell-type characteristics.</span></p> <p><strong><span lang="EN-US">Results</span></strong></p> <p><span lang="EN-US">NMF analysis identified three ASD subtypes. The three subtypes exhibited different phenotypic patterns: Cluster 1 had severe restricted and repetitive behaviors, Cluster 3 mainly had social communication impairments, Cluster 2 presented milder symptoms and better cognitive function. Differential expressed genes analysis linked Cluster 1 and Cluster3 to nervous system dysfunctions and morphogenesis of a branching structure, while Cluster 2 to immune system processes. The clusters also exhibited distinct gene expression patterns across brain regions, developmental stages, and cell types. Validation in two independent datasets confirmed the reproducibility of the distinct clusters.<strong> </strong></span></p> <p><strong><span lang="EN-US">Conclusions</span></strong></p> <p><span lang="EN-US">This molecular subtyping reveals biologically and clinically distinct subtypes of ASD, helping to understand the atypical mechanisms underlying ASD heterogeneity. It also contributes to the development of personalized therapeutic strategies for distinct subtypes. <span> </span></span></p>
title Transcriptomic Analysis in Autism Spectrum Disorder Suggests Three Molecular Subtypes with Distinct Phenotypic Profiles and Functional Pathways
url https://doi.org/10.5281/zenodo.19124179