Search Results - Mark Roberts
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Start, switch and stop (triple‐S) criteria for enzyme replacement therapy of late‐onset Pompe disease: European Pompe Consortium recommendation update 2024 Autoría: Benedikt Schoser, Nadine A. M. E. van der Beek, Alexander Broomfield, Esther Brusse, Jordi Diaz‐Manera, Andreas Hahn, Thomas Hundsberger, Cornelia Kornblum, Michelle Kruijshaar, Pascal Laforet, Eugen Mengel, Tiziana Mongini, David Orlikowski, Giancarlo Parenti, W. W. M. Pim Pijnappel, Mark Roberts, Thomas Scherer, Antonio Toscano, John Vissing, Johanna M. P. van den Hout, Pieter A. van Doorn, Stephan Wenninger, Ans T. van der Ploeg
Published 2024Fuente: Wiley Open AccessTipo de material: Artículo Open AccessAcceso al recurso